PPMD 2026 Annual Conference: Day 2: Gene Therapy - Today & Tomorrow

This session covers approved and investigational gene therapies (Elevidys, RGX-202, SGT-003, INS1201, PBGENE-DMD). Aravindhan Veerapandiyan, MD - Arkansas Children's Hospital Omer Abdul Hamid, MD - Nemours Children's Health Kevin Flanigan, MD, PhD - Nationwide Children's Hospital