Role of biomarkers meeting | MPS Society and IMPSN | Part 2 What does the science tell us?

The role of biomarkers in advancing access to treatments for individuals with neurocognitive or neuronopathic MPS conditions. Part 2 - What does the science tell us? (Rationale for Heparan sulfate as a biomarker) 00:33 Development of heparan sulfate assays - Frits Wijburg 11:35 Determining the origin of CSF heparan sulfate using biological compartment specific gene therapy - Grant Austin 21:16 Comparative and preclinical medicine - Matthew Ellinwood 31:24 The role of heparan sulfate in advancing clinical trial development - David Whiteman 48:02 Impact of trial failure on clinicians and patients - Spyros Batzios 58:21 Discussion