Gene Therapy in Sight: Chrissy Green of Finding Hope for Frizzle speaks to the UGDH community

Finding Hope for Frizzle (FRR1SL) has received orphan drug designation for their gene therapy program and are on track to dose the first patient in their community this year. Chrissy Green, co-founder and president, tells us their story and what it took to get to this point. As a recessive neurodevelopmental condition, Frizzle represents significant analogues for the UGDH community.

Brian Cox- The Fermi Paradox Will Change How You See The Universe
▶︎

Brian Cox- The Fermi Paradox Will Change How You See The Universe

UGDH: Clinical Features and Clinical Challenges in an Ultrarare Disorder | Dr. Kristin Barañano
▶︎

UGDH: Clinical Features and Clinical Challenges in an Ultrarare Disorder | Dr. Kristin Barañano

Удары по Wildberries и НПЗ. Ждать ли экономического краха? I Сергей Гуриев
▶︎

Удары по Wildberries и НПЗ. Ждать ли экономического краха? I Сергей Гуриев

Mick Jagger Can’t Name One Good Thing About Getting Older | The Interview
▶︎

Mick Jagger Can’t Name One Good Thing About Getting Older | The Interview

Understand AI in 14 minutes – with Anthropic's Chloe Lubinski [ARC 2026]
▶︎

Understand AI in 14 minutes – with Anthropic's Chloe Lubinski [ARC 2026]

This cell just changed biology
▶︎

This cell just changed biology

Your Phone Is Destroying Your Sense of Meaning | Arthur Brooks [ARC 2026]
▶︎

Your Phone Is Destroying Your Sense of Meaning | Arthur Brooks [ARC 2026]

Is Iran Becoming Another 'Forever War'? (w/ John Mearsheimer) | The Chris Hedges Report
▶︎

Is Iran Becoming Another 'Forever War'? (w/ John Mearsheimer) | The Chris Hedges Report

What is life? A Nobel Prize-winning scientist answers | Paul Nurse Full Interview
▶︎

What is life? A Nobel Prize-winning scientist answers | Paul Nurse Full Interview

The Most Famous (TV) Doctor Of All Time | Noah Wyle
▶︎

The Most Famous (TV) Doctor Of All Time | Noah Wyle

I Swapped Diets With A Victoria's Secret Model
▶︎

I Swapped Diets With A Victoria's Secret Model

Panel Discussion: Ann Vucic, Fr Dan Reehil, Mother Adela Galindo, Paul J Kim | Medjugorje Fest 2026
▶︎

Panel Discussion: Ann Vucic, Fr Dan Reehil, Mother Adela Galindo, Paul J Kim | Medjugorje Fest 2026

Pranks That Went Too Far in History
▶︎

Pranks That Went Too Far in History

UNPREDICTABLE Dancers Made The Judges Forget How To BLINK!
▶︎

UNPREDICTABLE Dancers Made The Judges Forget How To BLINK!

Maydorn's Opinion: Alphabet, Tesla, SpaceX, Micron, Nvidia, Nebius, IREN, Hut 8, Albemarle, Li-FT
▶︎

Maydorn's Opinion: Alphabet, Tesla, SpaceX, Micron, Nvidia, Nebius, IREN, Hut 8, Albemarle, Li-FT

Alex Hormozi’s Warning: Don’t Make These AI Businesses, They Will All Fail...
▶︎

Alex Hormozi’s Warning: Don’t Make These AI Businesses, They Will All Fail...

Denis Noble: "Neo-Darwinism Is Dead" | We Need A Biology Beyond Genes
▶︎

Denis Noble: "Neo-Darwinism Is Dead" | We Need A Biology Beyond Genes

Oprah with Belle Burden on the Collapse of Her 20 Year Marriage & Her Bestselling Memoir
▶︎

Oprah with Belle Burden on the Collapse of Her 20 Year Marriage & Her Bestselling Memoir

A Comprehensive Overview of Drug Development - Jacinthe Gingras, PhD - UGDH Family & Scientific Mtg
▶︎

A Comprehensive Overview of Drug Development - Jacinthe Gingras, PhD - UGDH Family & Scientific Mtg

Bluthochdruck SOFORT senken ohne Tabletten - 3 TOP Methoden
▶︎

Bluthochdruck SOFORT senken ohne Tabletten - 3 TOP Methoden