Josh’s Mullen test 6 months post gene therapy for Canavan disease.

Josh took the the Mullen test - a standardized developmental test for children ages 3–60 months that yields five subscale scores representing developmental ages: gross motor, fine motor, visual reception, expressive language, and receptive language, which allows for separate standard verbal and nonverbal summary scores to be constructed. The first time he took it before gene therapy he only got 45 minutes in before he could no longer answer the questions correctly. 6 months after his gene therapy trial he got 3 hours in, and only stopped because it was his dinner time and he was hungry! These are some highlights of how it went…. We are so amazed to be a part of history in finding a treatment for Canavan disease.